Discovery Portfolio
Prosensa’s broad RNA-modulation technology platform facilitates development of therapeutic molecules for a variety of genetic diseases, not limited to neuromuscular disorders. Prosensa collaborates with a selection of key academic institutions to apply its RNA modulation platform to other indications as well.
Initial proof of concept has been delivered and is further being investigated in cancer applications, immune disorders, bone and skin diseases. Prosensa will selectively partner these applications to progress the development of these programs.

Prosensa also focuses on improved oligochemistries and on both efficiency and delivery enhancing compounds.