Technology & products
Pipeline
RNA Modulation
Our RNA-modulating therapeutics aim at targeted modulation of gene expression employing single-stranded RNA-based antisense oligonucleotides (AONs).
Exon Skipping
Our exon skipping technology is based on interference with exon inclusion signals during the splicing of the pre-mRNA, in order to induce the skipping of the targeted exon from the mature mRNA (messenger RNA) and to increase the level of functional transcripts.
IP Portfolio
Prosensa has ensured a good level of IP protection for its lead products in DMD in both Europe and the US. In addition, Prosensa has developed or licensed a broad set of patent families covering pipeline products and discovery projects.